OUR WORK
Review and Analysis
Our team at Railroad Children is dedicated to working with patients, clinicians, and industry to identify novel treatments for even the rarest genetic diseases. Our comprehensive review and analysis of patient clinical records is an example of how we collaborate with experts in the field to provide solutions to medical problems and ensure that the latest advancements are utilized to their full potential.
Novel Treatments
At Railroad Children, we recognize that every patient is unique and requires individualized care. Our identification of novel treatments highlight our personalized approach to rare disease consulting, as we work with patients and their families to identify the best possible treatment options.
FDA Compassionate Use
Our team at Railroad Children is constantly pushing the boundaries of what is possible in the field of genetic disease consulting. Our approach to FDA Compassionate Use process is an example of how we leverage our expertise and partnerships to drive meaningful change by helping patients to access life changing care.